This story is republished from STAT, the health and medicine news site that’s a partner to the Globe. Sign up for STAT’s free Morning Rounds newsletter here. Cambridge-based Fulcrum Therapeutics said ...

Sickle cell disease—the subject of a new Seminar in The Lancet—is one of the most prevalent and fastest-growing genetic disorders worldwide. Although its true prevalence is difficult to determine ...

Fulcrum Therapeutics said Tuesday that an experimental pill for sickle cell disease increased levels of an alternate form of oxygen-carrying hemoglobin — interim results that suggest a simpler ...

This is the online version of ASH in 30 Seconds, STAT’s report from the American Society of Hematology meeting. Sign up for the email version here. It’s Day 2 of the ASH meeting. Let’s get straight ...

Nemours Children's Hospital is now offering Lyfgenia gene therapy. The treatment aims to reduce pain crises and hospital visits for young patients.

RICHMOND, Va. — September is National Sickle Cell Awareness Month. Sickle cell affects 100,000 people in the United States, primarily impacting African Americans. To learn more about the genetic blood ...

Serenity Cole enjoyed Christmas last month relaxing with her family near her St. Louis home, making crafts and visiting friends. It was a contrast to how Cole, 18, spent part of the 2024 holiday ...

Sickle cell disease is a hereditary condition, which means a person inherits it from their biological parents. The condition occurs when a person inherits two copies of the hemoglobin beta (HBB) gene ...